Gene therapy

Latest Stories in Gene therapy

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FDA approves Regeneron gene therapy to restore hearing for rare OTOF-related congenital deafness

Health

Apr 23, 2026

FDA approves Regeneron gene therapy to restore hearing for rare OTOF-related congenital deafness

The U.S. Food and Drug Administration approved the first gene therapy intended to restore hearing for people born deaf due to mutations in the OTOF gene. The therapy...

FDA Gene therapy OTOF-related genetic deafness

Study: Adeno-associated viral gene therapy restored hearing in most people with OTOF-related DFNB9; benefits persist more than two years for some

Health

Apr 22, 2026

Study: Adeno-associated viral gene therapy restored hearing in most people with OTOF-related DFNB9; benefits persist more than two years for some

A multinational research team led by investigators at Mass Eye and Ear and Fudan University reported results from a study of 42 children and adults (ages under 1 to ...

Medical Technology Gene therapy OTOF-related genetic deafness (DFNB9)